News & Insights

As evidence teams plan for 2026, expectations in rare diseases are shifting towards evidence that is carefully contextualised and clearly linked to decision-making needs. Recent guidance and industry commentary highlight the growing role of patient experience data, integrated real-world evidence, and earlier cross-functional planning, reinforcing that credibility comes from clarity and relevance rather than scale or complexity alone.

How can remote data collection methods be used in rare disease research?

Rare diseases are estimated to impact around 300 million people globally. The burden of rare diseases presents a global challenge by...

This article explains the importance and challenges of conducting Health Economics and Outcomes Research in Rare Diseases.